Current status and recent advances of gene therapy in hematological diseases
نویسندگان
چکیده
منابع مشابه
Recent Advances in Hemophilia Gene Therapy
Heterogeneous loss of function mutations at F8 and F9 genes causes X-linked recessive bleeding disorders, hemophilia A (HA) and hemophilia B (HB), respectively. HA is clinically indistinguishable from HB and accounts for more than 80% of hemophilia cases; the former affects 1/5000 and the latter 1/25000 male births worldwide. In Iran, it is estimated that around 4300 HA and 900 HB patients are ...
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ژورنال
عنوان ژورنال: International Journal of Hematology
سال: 2016
ISSN: 0925-5710,1865-3774
DOI: 10.1007/s12185-016-2036-9